Question

Gene therapy is an attempt to correct a genetic defect by providing a normal gene into the individual. By this the normal function can be restored. Alternate method would be to provide the gene product (protein/ enzyme) know as enzyme replacement therapy, which would also restore the function. Which in your opinion is a better option? Give reason for your answer

Answer 1

Gene therapy would be a better option because it has the potential to completely cure the patient. It is because the correct gene once introduced in the patient can continue to produce the correct protein/enzyme. Enzyme therapy does not offer permanent cure as it needs to be given to the patient on regular basis. It is also more expensive therapy.